Top 15 Pioneering Medical Biotechnology Companies
Top 15 Pioneering Medical Biotechnology Companies
The medical biotechnology industry is a sector that focuses on using biotechnology and pharmaceutical advancements to develop innovative treatments and therapies for various medical conditions. In this industry, there are companies specializing in genetic medicines, gene therapy research, and transformative treatments for genetic diseases. These companies aim to target the root causes of diseases and improve patients' lives by providing effective and personalized treatments. The industry is characterized by cutting-edge research and development, with a focus on advancements in RNA technologies, gene editing, and ex-vivo gene therapy. As the industry progresses, there is a growing emphasis on tackling complex health and societal challenges through the development of genetic medicines. The future of the medical biotechnology industry holds promising advancements in precision medicine and personalized therapies, ushering in a new era of healthcare.
Top 15 Medical Biotechnology Companies
1. Alnylam Pharmaceuticals
- Headquarter: Cambridge, Massachusetts, United States
- Founded: 2002
- Headcount: 1001-5000
- Latest funding type: Post Ipo Debt
Alnylam is a biotechnology and pharmaceutical company that specializes in genetic medicines for central nervous system and ocular diseases. They are known for their innovative RNAi therapeutics that silence the genes causing human disease. They are committed to tackling complex health and societal challenges through their medicines and actions.
2. BioMarin Pharmaceutical Inc.
- Headquarter: San Rafael, California, United States
- Founded: 1997
- Headcount: 1001-5000
- Latest funding type: Post Ipo Debt
BioMarin is a pharmaceutical company specializing in genetic therapies. They develop and provide transformative treatments for various genetic diseases, such as Morquio A Syndrome, PKU, and MPS. With a focus on gene therapy research, BioMarin aims to maximize the impact of genetic innovation and improve patients' lives.
3. bluebird bio
- Headquarter: Cambridge, Massachusetts, United States
- Founded: 1993
- Headcount: 1001-5000
- Latest funding type: Post Ipo Equity
Bluebird is a biotechnology company founded in 2010, specializing in ex-vivo gene therapy. With a focus on severe genetic diseases, they have industry-leading programs for sickle cell disease, β-thalassemia, and cerebral adrenoleukodystrophy.
4. Sarepta Therapeutics
- Headquarter: Cambridge, Massachusetts, United States
- Headcount: 501-1000
- Latest funding type: Post Ipo Equity
Sarepta Therapeutics is a biopharmaceutical company dedicated to developing and manufacturing innovative genetic medicines for rare diseases. Their focus areas include Duchenne Muscular Dystrophy, Limb-girdle Muscular Dystrophy, and Charcot-Marie-Tooth Disease. With expertise in gene therapy, RNA technologies, and gene editing, Sarepta is committed to transforming lives and providing hope for patients with rare diseases.
5. Ionis Pharmaceuticals, Inc.
- Headquarter: Carlsbad, California, United States
- Founded: 1989
- Headcount: 201-500
- Latest funding type: Post Ipo Debt
Ionis Pharmaceuticals is a biotechnology company focused on discovering, developing, and delivering genetic medicines that target the root causes of diseases. They aim to improve patients' lives by providing innovative treatments. With a strong commitment to scientific advancement, Ionis Pharmaceuticals remains at the forefront of medical research.
6. Centro de Ingeniería Genética y Biotecnología
- Headquarter: Playa, La Habana, Cuba
- Founded: 1986
- Headcount: 1001-5000
CIGB is a Cuban biotechnology company that focuses on the research, development, production, marketing, and export of innovative products in the field of genetic engineering and biotechnology. They specialize in vaccines, biopharmaceuticals, and diagnostic tests for the diagnosis, treatment, and prevention of diseases.
7. Amicus Therapeutics
- Headquarter: Philadelphia, Pennsylvania, United States
- Founded: 2002
- Headcount: 501-1000
- Latest funding type: Post Ipo Debt
Amicus Therapeutics is a biotechnology company at the forefront of advanced therapies for rare genetic diseases. They develop innovative treatments and leverage technology platforms to improve the lives of patients. Their pipeline includes programs for Fabry Disease, Pompe Disease, Batten Disease, and other rare diseases. They offer products like Galafold® and Amicus Assist™.
8. Abri
- Headquarter: Miami, Florida, United States
- Founded: 2007
- Headcount: 1001-5000
ABRI, Inc is a global integrated biotechnology and clinical research company offering clinical trial management solutions and bio-products. They provide audit support, collect biological materials, and offer outpatient clinic services and studies. ABRI operates with worldwide permits and certifications, collaborating with pharmaceutical sponsors and research organizations. They actively seek individuals to participate in clinical trials and contribute to medical innovations. ABRI is a trusted source of high-quality bio-products for customers in need of rare and highly characterized biological samples.
9. Agios Pharmaceuticals
- Headquarter: Cambridge, Massachusetts, United States
- Founded: 2008
- Headcount: 201-500
- Latest funding type: Series C
Agios is a leading company in the field of cellular metabolism, focusing on advancing therapies for patients with genetically defined diseases. Their pioneering leadership and unique understanding of the science drives their success in developing groundbreaking therapies. They prioritize patient needs and collaboration with healthcare professionals and partners to ensure their therapies have the biggest impact possible.
10. CRISPR Therapeutics
- Headquarter: Cambridge, Massachusetts, United States
- Founded: 2013
- Headcount: 201-500
- Latest funding type: Grant
CRISPR Therapeutics is a company that specializes in gene editing and cell therapies. They use the CRISPR/Cas9 therapeutic approach to treat genetically-defined diseases by editing cells inside the body.
11. Ascires
- Headquarter: Valencia/València, Comunidad Valenciana / Comunitat Valenciana, Spain
- Headcount: 501-1000
Ascires Grupo Biomédico is a leading company in the field of precision personalized medicine. With over 50 years of experience, we specialize in the development of biomarkers and diagnostic algorithms that integrate genomic, clinical, and imaging data. Our services include genetic testing, imaging diagnostics, and participation in medical, pharmaceutical, and scientific R&D projects. We strive to advance science and contribute to the improvement of healthcare by providing accurate diagnostics and personalized care across various medical specialties.
12. Lyell Immunopharma
- Headquarter: South San Francisco, California, United States
- Founded: 2018
- Headcount: 201-500
- Latest funding type: Series C
Lyell Immunopharma is a clinical-stage T-cell reprogramming company focused on developing curative cell therapies for patients with solid tumors. Their mission is to deliver transformative T-cell therapies that can go the distance for patients. They aim to address major barriers to successful adoptive cell therapy in solid tumors.
13. Sirnaomics
- Headquarter: Gaithersburg, Maryland, United States
- Founded: 2007
- Headcount: 51-200
- Latest funding type: Series E
Sirnaomics is a biotechnology company that specializes in RNAi therapeutics for the treatment of various diseases. They offer innovative solutions utilizing their GalNAc-based liver-targeting platforms and GalAhead™ programs. Sirnaomics is committed to developing cutting-edge therapies to improve patient outcomes.
14. 上海联合赛尔生物工程有限公司
- Headquarter: China
- Headcount: 201-500
United Biotech is a biotechnology company specializing in the research, development, manufacturing, and sales of genetically recombinant biological products and vaccines. They are committed to using innovation to create high-quality pharmaceutical and vaccine products for the betterment of society and humanity.
15. Modulight Corporation
- Headquarter: San Jose, California, United States
- Founded: 2000
- Headcount: 51-200
Modulight is a company specializing in lasers and optics for personalized medicine. They offer a range of products including laser solutions, illumination kits, and laser modules. Their expertise lies in drug delivery systems and they use light as a tool to control the delivery of drugs to target tissues. Modulight supports diagnostic applications and has a focus on ophthalmology, genetics, drug discovery, and high-value add applications.
Want to find more medical biotechnology companies?
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